First-pass extracted concept

RNA editing

Candidate: concept label2 source documents2 linked claims
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Evidence Snippets

We examine therapeutic applications spanning... RNA editing...
Evidence 1Source 1DOIPubMedprovenance
Nanomedicine-enhanced delivery of CRISPR-Cas13 for RNA editing in C9orf72-associated ALS.
Evidence 2Source 2DOIPubMedprovenance

Supporting Sources

Linked Claims

Claim 1application scopesupports2025Source 1DOIPubMed

Therapeutic applications discussed in the review span nuclear genome editing, mitochondrial genome modification, RNA editing, and epigenetic modulation, indicating expansion beyond traditional monogenic disorders.

Claim 2paper topicsupports2025Source 2DOIPubMed

The source concerns nanomedicine-enhanced delivery of CRISPR-Cas13 for RNA editing in C9orf72-associated ALS.